Project Title: Development Of Gene-Editing Therapy To Restore Type Vii Collagen For The Treatment Of RDEB Using A Topical RNP Crispr System
Thematic Area: Rare Skin Diseases
Focus of Research: Gene Therapy
Overview: This project aims to use novel non-viral, polymer-based gene therapy, with the potential to treat a broad range of severe genetic conditions. The first proof of concept therapy has been designed for the devastating genetic skin disease Epidermolysis Bullosa (EB), with the next target being Cystic Fibrosis
Funded by: EB Research Partnership Inc.
PI: Prof. Wenxin Wang
Other Group/team members: Dr Irene-Lara Saez
Project Duration: January 2020-September 2021
